Two of Opus's seven gene therapy assets are in clinical trials, with additional programs expected to enter the clinic.

Researchers from Radboud university medical center and University of Basel have discovered new genetic causes of inherited ...

The first patient has been dosed in a Phase 2 clinical trial testing RAG-17 in people with ALS who carry mutations in the ...

Researchers at the University of California have created a novel data structure and compression method that allows ...

Researchers have found that splitting the gene editor used in traditional CRISPR technology creates a more precise tool that can be switched on and off, with significantly less chance of causing ...

Sickle cell diseases arises from hemoglobin protein mutations. The mutation causes red blood cells to form a sickle shape rather than a round one. One study suggests that this mutation could be ...

PanMAN data structures compress pangenomes massively, encode evolutionary histories, and enable scalable analysis of millions of genomes.

Scientists have identified a genetic mutation in a gene called SHLP2, which encodes for a microprotein in mitochondria, and can reduce a carrier's likelihood of developing Parkinson's disease by 50 ...

The root causes of most forms of Alzheimer's disease largely remain a mystery. Now, researchers have revealed a new piece of the puzzle. Neurogeneticists at the University of Florida led by Lien ...

Engineers at the University of California have developed a new data structure and compression technique that enables the ...